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AVROBIO to Present New Clinical and Preclinical Data at the ASGCT 25th Annual Meeting
AVROBIO to Present New Clinical and Preclinical Data at the ASGCT 25th Annual Meeting
The planned presentations are listed below and the full preliminary program is available online at the ASGCT website.
ORAL PRESENTATION:
Hematopoietic stem cell gene therapy for cystinosis: updated results from a Phase 1/2 clinical trial
Oral Abstract Session on “Gene and Cell Therapy Trials in Progress”
POSTER PRESENTATION:
Long-term efficacy and safety in preclinical hematopoietic stem cell gene therapy in
Poster session on “Musculo-skeletal diseases”
About
Our vision is to bring personalized gene therapy to the world. We aim to prevent, halt or reverse disease throughout the body with a single dose of gene therapy designed to drive durable expression of therapeutic protein, even in hard-to-reach tissues and organs including brain, muscle and bone. AVROBIO’s pipeline is powered by our industry-leading plato® gene therapy platform, our foundation designed to deliver gene therapy worldwide. It includes clinical programs in cystinosis and Gaucher disease type 1, as well as preclinical programs in Gaucher disease type 3, Hunter syndrome and Pompe disease. We are headquartered in
Forward-Looking Statement
This press release contains forward-looking statements, including statements made pursuant to the safe harbor provisions of the Private Securities Litigation Reform Act of 1995. These statements may be identified by words and phrases such as “aims,” “anticipates,” “believes,” “could,” “designed to,” “estimates,” “expects,” “forecasts,” “goal,” “intends,” “may,” “plans,” “possible,” “potential,” “seeks,” “will,” and variations of these words and phrases or similar expressions that are intended to identify forward-looking statements. These forward-looking statements include, without limitation, statements regarding our business strategy for and the potential therapeutic benefits of our current and prospective product candidates, including the implementation of the plato® platform in our clinical trials and gene therapy programs. Any such statements in this press release that are not statements of historical fact may be deemed to be forward-looking statements. Results in preclinical or early-stage clinical trials may not be indicative of results from later stage or larger scale clinical trials and do not ensure regulatory approval. You should not place undue reliance on these statements, or the scientific data presented.
Any forward-looking statements in this press release are based on AVROBIO’s current expectations, estimates and projections about our industry as well as management’s current beliefs and expectations of future events only as of today and are subject to a number of risks and uncertainties that could cause actual results to differ materially and adversely from those set forth in or implied by such forward-looking statements. These risks and uncertainties include, but are not limited to, the risk that any one or more of AVROBIO’s product candidates will not be successfully developed or commercialized, the risk of cessation or delay of any ongoing or planned clinical trials of
1 Collaborator-sponsored Phase 1/2 clinical trial of AVR-RD-04 is funded in part by grants to
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Investor:
Westwicke, an
339-970-2843
chris.brinzey@westwicke.com
Media:
Ten
617-999-9620
krodophele@tenbridgecommunications.com
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